Treatment options for many rare and severe diseases have expanded rapidly in recent years thanks to groundbreaking research and significant technology breakthroughs.
The life sciences and pharmaceutical industry is constantly innovating to ensure that new treatments become available for patients.
One area that has seen particularly exciting progress is the genetic medicine space. Gene therapies and gene editing have opened the door to new, life-changing treatments for rare, inherited disorders that may have previously had a very inadequate standard of care.
They have offered hope of finding a cure for a range of diseases where that did not previously seem possible.
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